CRISPR/Cas9-Anwendungen bei seltenen Stoffwechselerkrankungen: Fortschritte in der Forschung
CRISPR/Cas9 technology is revolutionizing the treatment of rare metabolic diseases. This article explores the latest advancements in CRISPR/Cas9 applications, highlighting its potential to correct genetic defects, restore metabolic pathways, und die Patientenergebnisse verbessern.


