Targeting Beta-Globin Gene Mutations: CRISPR/Cas9 in Beta-Thalassemia Therapy
Beta-thalassemia, uma doença genética do sangue, is caused by mutations in the beta-globin gene. CRISPR/Cas9, a gene-editing technology, offers a promising approach for correcting these mutations and restoring normal hemoglobin production. This article analyzes the potential of CRISPR/Cas9 in beta-thalassemia therapy, exploring its advantages, limitações, e implicações futuras.












