Overcoming Genetic Blindness: CRISPR/Cas9 for Leber Congenital Amaurosis
CRISPR/Cas9 gene editing offers promising avenues for treating Leber congenital amaurosis (LCA), a genetic form of blindness, by targeting specific mutations and restoring vision. This revolutionary technology empowers researchers to correct genetic defects, potentially leading to cures for currently untreatable eye diseases.